Over a Decade of Innovation
We are pioneering a new era of medicines
Transforming the lives of patients living with serious diseases
Across a number of disease areas
1
Approved
Therapy
5
Clinical
Programs
10
Preclinical
Programs
Rapidly translating a revolutionary technology into therapies
Innovation that matters
Rapidly translating a revolutionary technology into therapies
Learn more about gene editingLearn more about our programs
We have established a diverse portfolio across a broad range of disease areas including hemoglobinopathies, oncology, diabetes and cardiovascular disease.
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